Encephalocele: Diagnosis to Treatment

What Is Encephalocele?

Brain encephalocele is a rare congenital cranial malformation in which a developmental fusion defect of the fetal skull bones allows brain tissue and/or its protective membranes to protrude outward through a bone defect. It is classified under neural tube defects (NTDs) and represents one of the severe forms of congenital central nervous system anomalies.

Neural tube closure normally occurs around the 3rd to 4th week of embryonic development. When this critical fusion process fails, an opening remains within the cranial bones, creating a pathway for herniation and leading to the formation of an encephalocele.

The content of the herniated sac varies; therefore, encephaloceles are divided into subtypes:

Types of Encephalocele

Meningocele: A sac containing only cerebrospinal fluid and meninges protrudes externally. No brain tissue is present within the sac.

Meningoencephalocele: Both meninges and brain tissue form the herniated sac. This is the most common encephalocele subtype.

Encephalomyelocele: A more severe form where both brain and spinal cord tissues herniate through the cranial defect.

Most cases present at birth with a visible, sac-like mass on the head and are frequently associated with additional structural anomalies.

Embryology and Pathophysiology

Failure of neural tube closure during early embryogenesis disrupts cranial bone formation and fusion. The resulting skull defect allows cerebrospinal fluid pressure to push neural tissues outward, forming a herniated sac.

The sac may contain:

Cerebrospinal fluid

Meninges

Brain parenchyma

In rare cases, vascular structures

The severity of clinical outcomes correlates strongly with the sac contents and associated intracranial abnormalities.

Anatomical Locations

Encephaloceles may occur in several cranial regions, including:

Occipital region

Frontonasal region

Parietal region

Bregmatic area

Rarely, Sphenoidal region

Etiology and Risk Factors

There is no single definitive cause of encephalocele. A multifactorial etiology involving genetic, environmental, and maternal metabolic factors is recognized.

Genetic and Chromosomal Associations

Encephalocele may occur with certain genetic syndromes and chromosomal anomalies, such as:

Trisomy 13 (Patau syndrome)

Trisomy 18 (Edwards syndrome)

Walker–Warburg syndrome

Knobloch syndrome

Roberts syndrome

Frontonasal dysplasia

Dissegmental dysplasia

Pseudo-Meckel syndrome

These conditions commonly feature craniofacial malformations and increased susceptibility to neural tube defects.

Environmental and Maternal Factors

Documented maternal risk contributors include:

Folate deficiency

Maternal diabetes

Teratogenic medication exposure (e.g., antiepileptics)

Alcohol and tobacco consumption

Radiation exposure

Amniotic band sequence

Maternal obesity

Among these, insufficient folic acid intake before conception and in early pregnancy is one of the strongest modifiable risk factors.

Clinical Features and Symptoms

The clinical presentation of encephalocele varies according to lesion size, sac contents, and associated brain malformations.

Local Signs

Externally visible cranial mass

Thinned or stretched overlying skin

Possible cerebrospinal fluid leakage

Craniofacial deformities

Neurological Manifestations

Intellectual disability

Global developmental delay

Motor dysfunction

Visual or auditory impairment

Hydrocephalus

Seizures

Brainstem-related symptoms

Symptom severity parallels the complexity of the herniated structures: Small meningoceles may produce minimal neurologic deficit, while large meningoencephaloceles are often associated with significant neurodevelopmental impairment.

Prenatal Diagnosis

Today, encephalocele can usually be detected during routine prenatal screening.

Ultrasonography

Identifies cranial bone defects

Demonstrates sac morphology and contents

Commonly visualized during second-trimester examinations

Fetal MRI

Superior in differentiating lesion contents

Guides postnatal surgical planning

It is also essential to evaluate for coexisting anomalies such as:

Hydrocephalus

Chiari malformation

Corpus callosum defects

Spinal abnormalities

Early diagnosis helps in parental counseling, pregnancy decision-making, and preparation for postnatal management.

Treatment Approach

Surgical Management

Surgery is the primary treatment for encephalocele. Goals of the operation include:

Removal of the herniated sac

Preservation of viable brain tissue

Secure closure of cerebrospinal fluid pathways

Reconstruction of cranial defects

Surgery is typically scheduled during early infancy, depending on lesion complexity and the baby’s clinical condition.

Postoperative and Long-Term Care

Hydrocephalus may develop, requiring ventriculoperitoneal shunting.

Long-term neurological rehabilitation is often needed.

Ongoing developmental screening and supportive treatment improve outcomes.